Duchenne Muscular Dystrophy clinical trials at UC Irvine

3 in progress, 0 open to eligible people

Showing trials for

  • Managed Access Program for Del-zota in Participants With DMD Mutations Amenable to Exon 44 Skipping

    Sorry, not accepting new patients

    The purpose of this Managed Access Program is to allow access to delpacibart zotadirsen (AOC 1044) for eligible patients diagnosed with DMD mutations amenable to exon 44 skipping. The patient's Administering Physician should follow the suggested treatment guidelines and comply with all local health authority regulations.

    Irvine, California and other locations

  • Extension of EDG-5506 in Participants With Becker Muscular Dystrophy

    Sorry, accepting new patients by invitation only

    EDG-5506-203 MESA is an open-label extension study to assess the long-term effect of sevasemten (EDG-5506) on safety, biomarkers, and functional measures in adults and adolescents with Becker muscular dystrophy

    Orange, California and other locations

  • Defining Endpoints in Becker Muscular Dystrophy

    Sorry, in progress, not accepting new patients

    This is a 24-month, observational study of 50 participants with Becker muscular dystrophy (BMD)

    Orange, California and other locations

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