Spinal Muscular Atrophy clinical trials at UC Irvine
1 research study open to eligible people
Showing trials for
Spinraza in Adult Spinal Muscular Atrophy
open to eligible people ages 18-70
This is a longitudinal, observational study of adult patients with genetically confirmed chromosome 5q SMA to examine the safety, tolerability, and effectiveness of SPINRAZA® (nusinersen) for up to 30 months.
Orange, California and other locations