Muscular Dystrophies clinical trials at UC Irvine
2 in progress, 1 open to eligible people
Showing trials for
AB-1003 (Previously LION-101) in Subjects With Genetic Confirmation of LGMD2I/R9 (Part1)
open to eligible people ages 18-65
The purpose of this study is to evaluate the safety and tolerability of a single intravenous infusion of AB-1003 in adults diagnosed with limb girdle muscular dystrophy type 2I/R9 (LGMD2I/R9). Participants will be treated in sequential, dose-level cohorts. (Part 1)
Irvine, California and other locations
Defining Endpoints in Becker Muscular Dystrophy
Sorry, in progress, not accepting new patients
This is a 24-month, observational study of 50 participants with Becker muscular dystrophy (BMD)
Orange, California and other locations
Our lead scientists for Muscular Dystrophies research studies include Tahseen Mozaffar, MD.
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