Skip to main content

Acid Maltase Deficiency clinical trials at UC Irvine

1 in progress, 0 open to eligible people

Showing trials for
  • A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)

    Sorry, in progress, not accepting new patients

    The purpose of this study is to evaluate the safety, tolerability, and efficacy of a single intravenous infusion of SPK-3006 in adults with clinically moderate, late-onset Pompe disease receiving enzyme replacement therapy (ERT). Participants will be treated in sequential, dose-level cohorts.

    Orange, California and other locations

Our lead scientists for Acid Maltase Deficiency research studies include .

Last updated: